Trial Details

RECRUITING
Basic Information
Clinical ID c3488
Identifier NCT01962415
Trial Title Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
Trial URL Visit Original Page
Study Information
Study Results

NO

Conditions Primary Immunodeficiency (PID)|Congenital Bone Marrow Failure Syndromes|Inherited Metabolic Disorders (IMD)|Hereditary Anemias|Inflammatory Conditions|Systemic Juvenile Idiopathic Arthritis (sJIA)|Juvenile Rheumatoid Arthritis (JRA)
Interventions DRUG: Hydroxyurea|DRUG: Alemtuzumab|DRUG: Fludarabine|DRUG: Melphalan|DRUG: Thiotepa
Participant Information
Sponsor Paul Szabolcs
City Pittsburgh
Country/Region United States
Enrollment Criteria
Sex Requirement ALL
Age Requirement CHILD, ADULT
Study Design
Study Type INTERVENTIONAL
Phase PHASE2
Time Information
Start Date 2014-02-04
Primary Completion Date 2026-11
Completion Date 2027-11