Drug ID:Drug112
Drug Name:Tofacitinib
CID:9926791
DrugBank ID:DB08895
Modality:Small Molecule
Groups:approved
US Approved:YES
Other Approved:YES
Identifier: NCT00787202, , NCT03281304, , NCT01458574, , NCT01470612, , NCT06625450, , NCT04424303, , NCT05112263, , NCT06095128, , NCT05728008, , NCT05431283, , NCT05313620, , NCT04925973, , NCT06780683, , NCT06274996, , NCT05782907, , NCT06095596, , NCT03653026, , NCT02819635, , NCT03345836, , NCT03006
Molecular Formula:C16H20N6O
Molecular Weight:312.37 g/mol
Isomeric SMILES:C[C@@H]1CCN(C[C@@H]1N(C)C2=NC=NC3=C2C=CN3)C(=O)CC#N
Synonyms:Tofacitinib; 477600-75-2; 3-((3R,4R)-4-methyl-3-(methyl(7H-pyrrolo[2,3-d]pyrimidin-4-yl)amino)piperidin-1-yl)-3-oxopropanenitrile; Cp-690 free base; tofacitinibum; UNII-87LA6FU830; CHEBI:71200; 87LA6FU830; CP-690550 FREE BASE; CP-690,550 FREE BASE
Phase 0: 6
Phase 1: 84
Phase 2: 131
Phase 3: 80
Phase 4: 39
Description:Tofacitinib is an inhibitor of Janus kinases, a group of intracellular enzymes involved in signaling pathways that affect hematopoiesis and immune cell function. It is approved by the FDA for treatment of moderate to severe rheumatoid arthritis that responds inadequately to methotrexate or in those who are intolerant to methotrexate. Besides rheumatoid arthritis, tofacitinib has also been studied in clinical trials for the prevention of organ transplant rejection, and the treatment of psoriasis and ulcerative colitis. Known adverse effects include nausea and headache as well as more serious immunologic and hematological adverse effects. Tofacitinib is marketed under the brand name Xeljanz.

Molecular Structure

2D Molecular Structure

Knowledge Graph

dtIDCIDCompound NameGene IDGene NameSpeciesPubMed IDsAction
dt948 9926791 Tofacitinib 2048 EPHB2 Homo sapiens (human) Inhibitor
dt949 9926791 Tofacitinib 6777 STAT5B Homo sapiens (human) None
dt950 9926791 Tofacitinib 3716 JAK1 Homo sapiens (human) Inhibitor
dt951 9926791 Tofacitinib 3718 JAK3 Homo sapiens (human) None
dt952 9926791 Tofacitinib 29110 TBK1 Homo sapiens (human) 25540906 None
dt953 9926791 Tofacitinib 3717 JAK2 Homo sapiens (human) 24417533 Inhibition
dt954 9926791 Tofacitinib 3718 JAK3 Homo sapiens (human) Inhibition
dt955 9926791 Tofacitinib 3718 JAK3 Homo sapiens (human) 24417533 Inhibition
dt956 9926791 Tofacitinib 3718 JAK3 Homo sapiens (human) 27572962 Inhibition
dt957 9926791 Tofacitinib 3716 JAK1 Homo sapiens (human) 24417533 Inhibition

  • No data available

Phase Distribution
Phase Description
  • Phase 0: Exploratory trials to assess drug behavior in humans
  • Phase 1: Safety trials to determine safe dosage range
  • Phase 2: Efficacy trials to evaluate therapeutic effects
  • Phase 3: Large-scale trials to confirm efficacy and safety
  • Phase 4: Post-marketing surveillance for long-term safety and efficacy

Trial IDTitlePhaseStatusSponsorIndicationsInterventions
NCT04624230 Evaluation of Oral Tofacitinib in Children Aged 2 to 17 Years Old Suffering From Moderate to Severe Ulcerative Colitis PHASE3 RECRUITING Pfizer Ulcerative Colitis DRUG: tofacitinib Details
NCT01465763 A Study Evaluating The Efficacy And Safety Of CP-690,550 In Patients With Moderate To Severe Ulcerative Colitis PHASE3 COMPLETED Pfizer Ulcerative Colitis DRUG: tofacitinib|DRUG: Placebo Details
NCT04032756 Tofacitinib Registry of Patients With Ulcerative Colitis in Germany None TERMINATED Ced Service GmbH Colitis, Ulcerative|Biologics|Tofacitiniib|Chroni… None Details
NCT01458951 A Study To Evaluate Both The Efficacy and Safety Profile of CP-690,550 In Patients With Moderately to Severely Active Ulcerative Colitis PHASE3 COMPLETED Pfizer Ulcerative Colitis DRUG: tofacitinib|DRUG: Placebo Details
NCT05112263 Tofacitinib Versus Cyclosporine for Steroid Refractory Acute Severe Ulcerative Colitis None NOT_YET_RECRUITING Post Graduate Institute of Medical Education and Research, Chandigarh Ulcerative Colitis DRUG: Tofacitinib|DRUG: Cyclosporine Details
NCT06469424 An Active Surveillance, Post-Authorization Study to Characterize the Safety of Tofacitinib in Patients With Moderately to Severely Active Ulcerative Colitis in the Real-World Setting Using Data From the United Registries for Clinical Assessment and Research (UR-CARE) in the European Union (EU) None RECRUITING Grupo Espanol de Trabajo en Enfermedad de Crohn y Colitis Ulcerosa Ulcerative Colitis None Details
NCT06095128 A Study of Vedolizumab With Tofacitinib in Adults With Ulcerative Colitis (UC) PHASE4 RECRUITING Takeda Ulcerative Colitis DRUG: Vedolizumab|DRUG: Tofacitinib Details
NCT05728008 Retrospective Observational Comparison Study Between Ustekinumab and Tofacitinib as Third Line Therapy in a Multicenter Cohort of Patients With Refractory Ulcerative Colitis. None COMPLETED IRCCS San Raffaele Ulcerative Colitis DRUG: Ustekinumab|DRUG: Tofacitinib Details
NCT04743518 Impact of Anti-TNF, Vedolizumab and Tofacitinib on Aortic Stiffness, Carotid Intima-media Thickness and Cardiovascular Risk of Patients With Ulcerative Colitis None UNKNOWN Centre Hospitalier Universitaire, Amiens Ulcerative Colitis OTHER: Aortic pulse wave velocity|OTHER: carotid … Details
NCT05104723 Safety and Efficacy of Tofacitinib for Chronic Granulomatous Disease With Inflammatory Complications PHASE1|PHASE2 ENROLLING_BY_INVITATION National Institute of Allergy and Infectious Diseases (NIAID) Chronic Granulomatous Disease|Inflammatory Gastro… DRUG: XELJANZ (tofacitinib) Details
NCT05431283 Real-world Effectiveness of Tofacitinib on Ulcerative Colitis Associated Spondyloarthropathy None UNKNOWN Italian Group for the study of Inflammatory Bowel Disease (IG-IBD) Ulcerative Colitis|Spondyloarthropathy DRUG: Tofacitinib Details
NCT03103412 TD-3504 SAD in Healthy Subjects and Subjects With Ulcerative Colitis (UC) PHASE1 COMPLETED Theravance Biopharma Active Mild Ulcerative Colitis, Active Moderate U… DRUG: TD-3504|DRUG: 15N2-tofacitinib|DRUG: Placebo Details
NCT05069259 Generate Real World Data On Tofacitinib Induction Therapy and Changes In Clinical and Patient Reported Outcomes. None TERMINATED Pfizer Ulcerative Colitis OTHER: Stool sample collection Details
NCT03663400 Identify Predictors That Distinguish Between Tofacitinib Responders and Non-responders Based on Genotype and Cellular and Molecular Profiles From Pinch Biopsies, Blood and Stool Samples None COMPLETED NYU Langone Health Ulcerative Colitis DIAGNOSTIC_TEST: GWAS analysis by Illumina BeadCh… Details
NCT05313620 Effect of Tofacitinib on Coagulation and Platelet Function, and Its Role in Thromboembolic Events PHASE4 RECRUITING Fundación de Investigación Biomédica - Hospital Universitario de La Princesa Ulcerative Colitis|Thromboembolism DRUG: Tofacitinib|DRUG: Infliximab Adalimumab y G… Details
CTRI/2024/01/061649 Prevalence and impact of sarcopenia and frailty in inflammatory bowel disease, and the effect of multi-modal interventions on sarcopenia and clinical outcomes in patients with inflammatory bowel disease - NIL PHASE3 Not Recruiting All India Institute of Medical Sciences Health Condition 1: K509- Crohns disease, unspeci… Intervention1: High protein anti-inflammatory die… Details
CTRI/2023/10/058514 Evaluation of effectiveness and safety of oral tofacitinib in patients with Parthenium dermatitis: A prospective interventional open label study - NIL Not Available Not Recruiting AIIMS, New Delhi Health Condition 1: L237- Allergic contact dermat… Intervention1: Oral Tofacitinib: Tofacitinib is a… Details
ISRCTN96296121 Defining microbial predictors of responsiveness to biologic therapies in Crohn disease and ulcerative colitis Not Available Recruiting Newcastle upon Tyne Hospitals NHS Foundation Trust Crohn disease and ulcerative colitis Digestive S… Current interventions as of 19/12/2024: This is… Details
ISRCTN13495664 SARS-CoV2 Vaccination immunogenicity in Immunosuppressed inflammatory bowel disease Patients Not Available Not Recruiting Imperial College London Immune responses to SARS-CoV-2 vaccination in imm… 600 IBD patients will be recruited stratified acc… Details
CTRI/2021/10/037641 An open label study to compare the efficacy and safety of tofacitinib compared to corticosteroids for inducing remission in moderately severe active ulcerative colitis PHASE4 Recruiting Dayanand Medical College and Hospital Ludhiana Disease.2. Total mayo clinic score <6 or >9. 3.… Health Condition 1: K51- Ulcerative colitis Details

Disease IDDisease NameDefinitionCategoryRelated DrugsMechanism
No data available

Strategy IDTherapeutic StrategySynonymsRelated DrugsMechanism
S07 Blockade of cytokine Cytokine signalling apremilast; roflumilast; filgotinib; tofacitinib; ABT494; ABT-874; ustekinumab; isankizumab; LY-2525623; AMG139; MEDI2079; guselkumab Various T-cell subsets, their differentiation pathways and … Details

Upfront tofacitinib in patients with biological-naïve ulcerative colitis - An I…

PMID: 37726491
Year: 2024
Relationship Type: Treatment Score: 6.5

OBJECTIVES: Tofacitinib is a Janus Kinase inhibitor used for treating moderate to severe ulcerative colitis (UC), mainly after the failure of biologi…

Experience with Tofacitinib in Patients with Ulcerative Colitis: Data from a Un…

PMID: 37639057
Year: 2023
Relationship Type: Treatment Score: 6.5

BACKGROUND: Tofacitinib is an oral small molecule Janus kinase inhibitor for the treatment of ulcerative colitis (UC). AIMS: To evaluate real-world d…

Outcomes of Tofacitinib Use in an Irish Pediatric Cohort

PMID: 37600624
Year: 2023
Relationship Type: Treatment Score: 6.5

BACKGROUND: Pediatric ulcerative colitis (UC) is typically more extensive and severe at diagnosis compared with adult disease. Tofacitinib, a Janus k…

Outcomes out to 12 months after sequential use of high-dose tofacitinib followi…

PMID: 37599224
Year: 2023
Relationship Type: Treatment Score: 6.5

Acute severe colitis (ASUC) remains a significant cause of morbidity in up to 25% of patients with ulcerative colitis during their disease course. We…

Presence of risk factors associated with colectomy among patients with ulcerati…

PMID: 37560161
Year: 2023
Relationship Type: Treatment Score: 6.5

BACKGROUND: Tofacitinib is an oral small molecule Janus kinase inhibitor for the treatment of ulcerative colitis (UC). OBJECTIVE: To assess colectomy…

Real-Life Efficacy of Tofacitinib in Various Situations in Ulcerative Colitis: …

PMID: 37542737
Year: 2024
Relationship Type: Treatment Score: 6.5

BACKGROUND AND AIMS: Tofacitinib (TFB) appears to be effective in the treatment of ulcerative colitis (UC); however, available real-world studies are…

Tofacitinib-induced eosinophilia

PMID: 37539549
Year: 2023
Relationship Type: Treatment Score: 6.5

Tofacitinib is an oral small molecule JAK inhibitor approved for the treatment of moderate to severe ulcerative colitis (UC). Its efficacy and safety…

Modeling of Treatment Outcomes with Tofacitinib Maintenance Therapy in Patients…

PMID: 37525075
Year: 2023
Relationship Type: Treatment Score: 6.5

INTRODUCTION: Tofacitinib is an oral small molecule Janus kinase inhibitor for the treatment of ulcerative colitis (UC). This post hoc analysis asses…

P004 Steroid-Free Remission in Patients With Ulcerative Colitis Receiving Tofac…

PMID: 37461925
Year: 2021
Relationship Type: Treatment Score: 6.5

BACKGROUND: Tofacitinib is a selective immunosuppressant, the first representative of the inhibitors of the janus kinase family, which has high selec…

Major Adverse Cardiovascular Events by Baseline Cardiovascular Risk in Patients…

PMID: 37402275
Year: 2023
Relationship Type: Treatment Score: 6.5

BACKGROUND AND AIMS: Patients with inflammatory bowel disease have increased risk of atherosclerotic cardiovascular [CV] disease [ASCVD]. Tofacitinib…

Manifestation of acute appendicitis as known but paradox visceral side effect o…

PMID: 37393666
Year: 2023
Relationship Type: Treatment Score: 6.5

BACKGROUND: The etiopathogenesis of accompanying inflammatory phenomena and consequences of immunomodulation constitute a challenging and innovative …

Use of tofacitinib as first or second-line therapy is associated with better ou…

PMID: 37358928
Year: 2023
Relationship Type: Treatment Score: 6.5

BACKGROUND: Data regarding the real-world (RW) use of tofacitinib (TOF) in patients with ulcerative colitis (UC) are limited. We aimed to investigate…

Comparing Patient-Reported Outcomes Among Anti-TNF Experienced Patients With Ul…

PMID: 37350775
Year: 2023
Relationship Type: Treatment Score: 6.5

BACKGROUND: Primary and secondary nonresponse to anti-tumor necrosis factor (TNF) therapy is common in patients with ulcerative colitis (UC), yet lim…

The current role of Tofacitinib in acute severe ulcerative colitis in adult pat…

PMID: 37316363
Year: 2023
Relationship Type: Treatment Score: 6.5

BACKGROUND: Despite rescue therapy, acute severe ulcerative colitis (ASUC) is associated with a high risk of colectomy, while treatment options remai…

Impact of biological agents and tofacitinib for moderate-to-severe ulcerative c…

PMID: 37313882
Year: 2021
Relationship Type: Treatment Score: 6.5

INTRODUCTION: In the past few years, several options have been proposed as alternative and more effective therapeutic drugs for moderate-to-severe ul…

Delayed and limited administration of the JAKinib tofacitinib mitigates chronic…

PMID: 37275854
Year: 2023
Relationship Type: Treatment Score: 6.5

In inflammatory bowel disease, dysregulated T cells express pro-inflammatory cytokines. Using a chronic azoxymethane (AOM)/dextran sulfate sodium (DS…

Real-World Experience With Tofacitinib Dose De-Escalation in Patients With Mode…

PMID: 37187323
Year: 2023
Relationship Type: Treatment Score: 6.5

BACKGROUND & AIMS: Tofacitinib is associated with sustained steroid-free remission in patients with ulcerative colitis (UC), with the lowest effectiv…

Tofacitinib to Treat Severe Acute Refractory Colitis in a Teenager: Case Report…

PMID: 37168636
Year: 2022
Relationship Type: Treatment Score: 6.5

Acute severe colitis (ASC) may occur within 3 months of ulcerative colitis diagnosis in 9%-15% of children and the rate of colectomy is up to 40%-50%…

Comparative Efficacy of Infliximab Versus Tofacitinib for Inducing Remission in…

PMID: 37119375
Year: 2023
Relationship Type: Treatment Score: 6.5

OBJECTIVE: In the absence of head-to-head clinical trials, indirect comparative studies are needed to help position therapies in ulcerative colitis (…

Tofacitinib experience in patients with enteropathic arthritis

PMID: 37009645
Year: 2023
Relationship Type: Treatment Score: 6.5

Background/aim: The JAK-STAT pathway is involved in the pathogenesis of both the inflammatory bowel disease (IBD) and spondyloarthropathy group of di…

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