Drug ID:Drug16
Drug Name:Cyclophosphamide
CID:2907
DrugBank ID:DB00531
Modality:Small Molecule
Groups:approved|investigational
US Approved:YES
Other Approved:YES
Identifier: NCT03219359
Molecular Formula:C7H15Cl2N2O2P
Molecular Weight:261.08 g/mol
Isomeric SMILES:C1CNP(=O)(OC1)N(CCCl)CCCl
Synonyms:cyclophosphamide; 50-18-0; Cytoxan; Cyclophosphamid; Cyclophosphane; Endoxan; Cytophosphan; Procytox; Sendoxan; Clafen
Phase 0: 66
Phase 1: 1168
Phase 2: 2257
Phase 3: 818
Phase 4: 97
Description:Precursor of an alkylating nitrogen mustard antineoplastic and immunosuppressive agent that must be activated in the liver to form the active aldophosphamide. It has been used in the treatment of lymphoma and leukemia. Its side effect, alopecia, has been used for defleecing sheep. Cyclophosphamide may also cause sterility, birth defects, mutations, and cancer. [PubChem]

Molecular Structure

2D Molecular Structure

Knowledge Graph

dtIDCIDCompound NameGene IDGene NameSpeciesPubMed IDsAction
dt139 2907 Cyclophosphamide 7150 TOP1 Homo sapiens (human) None
dt140 2907 Cyclophosphamide 4908 NTF3 Homo sapiens (human) None
dt141 2907 Cyclophosphamide 7132 TNFRSF1A Homo sapiens (human) None
dt142 2907 Cyclophosphamide 3458 IFNG Homo sapiens (human) None
dt143 2907 Cyclophosphamide 4613 MYCN Homo sapiens (human) None
dt144 2907 Cyclophosphamide 1565 CYP2D6 Homo sapiens (human) None
dt145 2907 Cyclophosphamide 5595 MAPK3 Homo sapiens (human) None
dt146 2907 Cyclophosphamide 1557 CYP2C19 Homo sapiens (human) None
dt147 2907 Cyclophosphamide 2099 ESR1 Homo sapiens (human) 23611293 None
dt148 2907 Cyclophosphamide 22809 ATF5 Homo sapiens (human) None

  • No data available

Phase Distribution
Phase Description
  • Phase 0: Exploratory trials to assess drug behavior in humans
  • Phase 1: Safety trials to determine safe dosage range
  • Phase 2: Efficacy trials to evaluate therapeutic effects
  • Phase 3: Large-scale trials to confirm efficacy and safety
  • Phase 4: Post-marketing surveillance for long-term safety and efficacy

Trial IDTitlePhaseStatusSponsorIndicationsInterventions
NCT03219359 Autologous Stem Cell Transplant for Crohn's Disease PHASE2 RECRUITING Aaron Etra Crohn Disease PROCEDURE: Autologous stem cell transplant|DRUG: … Details

Disease IDDisease NameDefinitionCategoryRelated DrugsMechanism
No data available

Strategy IDTherapeutic StrategySynonymsRelated DrugsMechanism
No data available

Prospective Study of Allogeneic Hematopoietic Stem Cell Transplantation with Po…

PMID: 32798657
Year: 2020
Relationship Type: Treatment Score: 9.5

Allogeneic hematopoietic stem cell transplantation (HSCT) is performed as a curative treatment for children with nonmalignant diseases, such as bone …

Safety and efficacy of intravenous cyclophosphamide pulse therapy in therapy re…

PMID: 28456770
Year: 2017
Relationship Type: Treatment Score: 9.3

A major challenge in the management of persistently active Crohn's disease patient's refractory to treatment regimen following the current guidelines…

Remission of refractory Crohn's disease by high-dose cyclophosphamide and autol…

PMID: 22937722
Year: 2012
Relationship Type: Treatment Score: 9.1

BACKGROUND: Despite advances in immunosuppressive therapy, up to 10% of patients with severe Crohn's disease (CD) remain refractory to conventional t…

Cyclophosphamide therapy in Sweet's syndrome complicating refractory Crohn's di…

PMID: 22115387
Year: 2011
Relationship Type: Treatment Score: 9.1

BACKGROUND: Sweet's syndrome is a rare extraintestinal manifestation of Crohn's disease that is usually treated by corticosteroids. Cyclophosphamide …

Transformative Results in Giant Pyoderma Gangrenosum with Dexamethasone-cycloph…

PMID: 40069562
Year: 2025
Relationship Type: Treatment Score: 6.5

Pyoderma gangrenosum (PG) is a cutaneous ulcerative condition that can present in various forms, including ulcerative, bullous, pustular, vegetative,…

Cyclophosphamide-free Mobilisation Increases Safety While Preserving the Effica…

PMID: 38757210
Year: 2024
Relationship Type: Association Score: 6.5

Autologous stem cell transplantation with low-dose cyclophosphamide to improve …

PMID: 38408175
Year: 2024
Relationship Type: Association Score: 6.5

Cyclophosphamide Pulse Therapy in Severe Refractory Crohn's Disease: A Retrospe…

PMID: 30018965
Year: 2018
Relationship Type: Treatment Score: 6.3

OBJECTIVE To identify the factors associated with first Clostridium difficile infection (CDI) that predict fecal microbiota transplantation (FMT) fo…

Complete resolution of severe ulcerative colitis after haploidentical hematopoi…

PMID: 28581471
Year: 2017
Relationship Type: Association Score: 6.3

Pathogenesis of infectious bursal disease in cyclophosphamide-treated chickens

PMID: 18670979
Year: 1992
Relationship Type: Association Score: 6.1

BACKGROUND: There has been little investigation of fatigue, a common symptom in inflammatory bowel disease (IBD). The aim of this study was to evalu…

Pulse cyclophosphamide therapy for inflammatory bowel disease

PMID: 16534885
Year: 2006
Relationship Type: Treatment Score: 6.1

The central issue for Genetic Analysis Workshop 14 (GAW14) is the question, which is the better strategy for linkage analysis, the use of single-nuc…

Safety and efficacy of intravenous pulse cyclophosphamide in acute steroid refr…

PMID: 12584219
Year: 2003
Relationship Type: Association Score: 6.1

Using a disease specific instrument to measure the health related quality of life (HRQOL) of patients with inflammatory bowel disease (IBD), it has …

Response of the chicken bursal stroma to treatment with cyclophosphamide and IB…

PMID: 2855388
Year: 1988
Relationship Type: Treatment Score: 6.1

Chronic inflammatory T-cell-mediated diseases such as inflammatory bowel disease (IBD) are often treated with immunosuppressants including corticost…