Drug ID:Drug27
Drug Name:Metformin
CID:4091
DrugBank ID:DB00331
Modality:Small Molecule
Groups:approved
US Approved:YES
Other Approved:YES
Identifier: NCT05553704, , NCT05574387, , NCT03986996
Molecular Formula:C4H11N5
Molecular Weight:129.16 g/mol
Isomeric SMILES:CN(C)C(=N)N=C(N)N
Synonyms:metformin; 657-24-9; 1,1-Dimethylbiguanide; N,N-dimethylimidodicarbonimidic diamide; Fluamine; Metformine; Metiguanide; Imidodicarbonimidic diamide, N,N-dimethyl-; Dimethylbiguanide; Flumamine
Phase 0: 58
Phase 1: 745
Phase 2: 530
Phase 3: 564
Phase 4: 555
Description:Metformin is a biguanide antihyperglycemic agent used for treating non-insulin-dependent diabetes mellitus (NIDDM). It improves glycemic control by decreasing hepatic glucose production, decreasing glucose absorption and increasing insulin-mediated glucose uptake. Metformin is the only oral antihyperglycemic agent that is not associated with weight gain. Metformin may induce weight loss and is the drug of choice for obese NIDDM patients. When used alone, metformin does not cause hypoglycemia; however, it may potentiate the hypoglycemic effects of sulfonylureas and insulin. Its main side effects are dyspepsia, nausea and diarrhea. Dose titration and/or use of smaller divided doses may decrease side effects. Metformin should be avoided in those with severely compromised renal function (creatinine clearance < 30 ml/min), acute/decompensated heart failure, severe liver disease and for 48 hours after the use of iodinated contrast dyes due to the risk of lactic acidosis. Lower doses should be used in the elderly and those with decreased renal function. Metformin decreases fasting plasma glucose, postprandial blood glucose and glycosolated hemoglobin (HbA1c) levels, which are reflective of the last 8-10 weeks of glucose control. Metformin may also have a positive effect on lipid levels. In 2012, a combination tablet of linagliptin plus metformin hydrochloride was marketed under the name Jentadueto for use in patients when treatment with both linagliptin and metformin is appropriate.

Molecular Structure

2D Molecular Structure

Knowledge Graph

dtIDCIDCompound NameGene IDGene NameSpeciesPubMed IDsAction
dt248 4091 Metformin 5604 MAP2K1 Homo sapiens (human) None
dt249 4091 Metformin 6794 STK11 Homo sapiens (human) None
dt250 4091 Metformin 5728 PTEN Homo sapiens (human) None
dt251 4091 Metformin 5290 PIK3CA Homo sapiens (human) None
dt252 4091 Metformin 3265 HRAS Homo sapiens (human) None
dt253 4091 Metformin 5465 PPARA Homo sapiens (human) None
dt254 4091 Metformin 55244 SLC47A1 Homo sapiens (human) 37713619 Modulator
dt255 4091 Metformin 32 ACACB Homo sapiens (human) 37713619 Activator
dt256 4091 Metformin 2110 ETFDH Homo sapiens (human) Inhibitor
dt257 4091 Metformin 5564 PRKAB1 Homo sapiens (human) Inducer|Activator

  • No data available

Phase Distribution
Phase Description
  • Phase 0: Exploratory trials to assess drug behavior in humans
  • Phase 1: Safety trials to determine safe dosage range
  • Phase 2: Efficacy trials to evaluate therapeutic effects
  • Phase 3: Large-scale trials to confirm efficacy and safety
  • Phase 4: Post-marketing surveillance for long-term safety and efficacy

Trial IDTitlePhaseStatusSponsorIndicationsInterventions
NCT05553704 Metformin in Patients With Ulcerative Colitis Treated With Mesalamine PHASE2 COMPLETED Tanta University Inflammatory Bowel Diseases DRUG: Metformin Details
NCT05574387 Metformin as Added on Therapy in Patients With Ulcerative Colitis PHASE2 RECRUITING Tanta University Inflammatory Bowel Diseases DRUG: Metformin Details
NCT04750135 Assessment of Metformin as Adjuvant Therapy in Patients With Ulcerative Colitis PHASE2 UNKNOWN National Hepatology & Tropical Medicine Research Institute Ulcerative Colitis|Inflammatory Bowel Diseases DRUG: metformin 500 mg TID Oral Tablet|DRUG: Plac… Details
NCT04624230 Evaluation of Oral Tofacitinib in Children Aged 2 to 17 Years Old Suffering From Moderate to Severe Ulcerative Colitis PHASE3 RECRUITING Pfizer Ulcerative Colitis DRUG: tofacitinib Details
NCT06651281 Extension Study of Long-term Safety and Efficacy of Tulisokibart in Participants With Crohn's Disease or Ulcerative Colitis (MK-7240-011) PHASE3 RECRUITING Merck Sharp & Dohme LLC Crohn Disease|Colitis, Ulcerative DRUG: Tulisokibart|DRUG: Placebo to tulisokibart Details
NCT04857112 Study Evaluating Efficacy and Safety of Amiselimod (MT-1303) in Mild to Moderate Ulcerative Colitis PHASE2 ACTIVE_NOT_RECRUITING Bausch Health Americas, Inc. Ulcerative Colitis DRUG: Low Dose MT-1303|DRUG: High Dose MT-1303|DR… Details
NCT05986136 Activation of Autophagy and Suppression of Apoptosis by Dapagliflozin Attenuates Inflammatory Bowel Disease PHASE2|PHASE3 RECRUITING Mostafa Bahaa Inflammatory Bowel Diseases DRUG: Mesalamine|DRUG: Dapagliflozin 10mg Tab Details
NCT06353828 Phase 2a Study to Evaluate IcBD-01 Enema in Active Ulcerative Colitis Patients PHASE2 ACTIVE_NOT_RECRUITING CannaMore Biotechs Ulcerative Colitis DRUG: CBD, synthetic form|DRUG: Placebo Details
NCT04478825 Efficacy and Safety of Rectally Administered BBT-401-1S in Subjects With Ulcerative Colitis PHASE1 TERMINATED Bridge Biotherapeutics, Inc. Ulcerative Colitis DRUG: BBT-401-1S Details
NCT06570772 Study to Investigate Comparative Efficacy, Safety and Immunogenicity Between AVT16 and Entyvio PHASE3 RECRUITING Alvotech Swiss AG Ulcerative Colitis BIOLOGICAL: AVT16|BIOLOGICAL: Vedolizumab Details
NCT01290042 Study to Evaluate Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of AMG 181. PHASE1 COMPLETED Amgen Ulcerative Colitis|Crohn's Disease DRUG: AMG 181|OTHER: Placebo for AMG 181 Details
NCT05507203 ABTECT-1 - ABX464 Treatment Evaluation for Ulcerative Colitis Therapy -1 PHASE3 RECRUITING Abivax S.A. Ulcerative Colitis DRUG: ABX464|DRUG: Placebo Details
NCT00207688 A Long Term Safety Study of Infliximab (Remicade) in in Ulcerative Colitis Patients None COMPLETED Janssen Research & Development, LLC Ulcerative Colitis DRUG: Infliximab 5 mg/kg|DRUG: Infliximab 10 mg/k… Details
NCT04677179 A Study of LY3471851 in Adult Participants With Moderately to Severely Active Ulcerative Colitis (UC) PHASE2 TERMINATED Nektar Therapeutics Colitis, Ulcerative DRUG: LY3471851|DRUG: Placebo Details
NCT02611830 Efficacy and Safety of Vedolizumab Subcutaneously (SC) as Maintenance Therapy in Ulcerative Colitis PHASE3 COMPLETED Takeda Colitis, Ulcerative DRUG: Vedolizumab 300 mg IV|DRUG: Placebo IV|DRUG… Details
NCT02958865 Study to Compare Oral PF-06651600, PF-06700841 and Placebo in Subjects With Moderate to Severe Ulcerative Colitis PHASE2 COMPLETED Pfizer Ulcerative Colitis DRUG: PF-06651600 or Placebo|DRUG: PF-06700841 or… Details
NCT06420492 Study of Novel Therapeutics for Acute Remedy of Colitis PHASE2 NOT_YET_RECRUITING Brigham and Women's Hospital Ulcerative Colitis|Ulcerative Colitis Chronic Mod… DRUG: BRS201 Details
NCT03943550 Double-Blinded, Placebo-Controlled Phase 1b Study for Safety, PK, Efficacy, PD of RO7049665 in Participants With Ulcerative Colitis (UC) PHASE1 TERMINATED Hoffmann-La Roche Ulcerative Colitis DRUG: RO7049665|DRUG: Placebo Details
NCT04133194 Adherence of a 1.600 mg Single Tablet 5-ASA Treatment of Ulcerative Colitis PHASE4 RECRUITING Flemming Bendtsen Ulcerative Colitis DRUG: Mesalazine|DRUG: Mesalazine Details
NCT02392221 Impact of Therapeutic Strategies in the Pediatric Inflammatory Bowel Disease: a Population Based Study (1988-2011). None COMPLETED Centre Hospitalier Universitaire, Amiens Pediatric Inflammatory Bowel Disease None Details

Disease IDDisease NameDefinitionCategoryRelated DrugsMechanism
1.0 Crohn's disease An intestinal disease that involves inflammation located_in intestine. disease of anatomical entity gastrointestinal system disease, intestinal disease, inflammatory bowel disease Obiltoxaximab; Budesonide; Hydrocortisone acetate; Sulfasalazine; Ursodeoxycholic acid; Pegunigalsidase alfa; Imiglucerase; Bictegravir; Taliglucerase alfa; Etelcalcetide; Cimetidine; Desonide Crohn's disease is a relapsing systemic inflammatory diseas… Details

Strategy IDTherapeutic StrategySynonymsRelated DrugsMechanism
S01 Anti-inflammatory inflammatory 5-Aminosalicylates (5-ASAs); corticosteroids Crohn's disease and ulcerative colitis are the two main com… Details
S02 Immunosuppression Classic immunosuppressive drugs azathioprine; 6-mercaptopurine; methotrexate; ciclosporin-A; tacrolimus Ciclosporin-A and tacrolimus bind to specific intracellular… Details
S03 Anti-TNF agents Tumor necrosis factor infliximab; adalimumab; golimumab; certolizumab pegol TNF is produced by various immune and non-immune cells in t… Details
S04 T-cell homing and retention T-cell trafficking vedolizumab; anti-MAdCAM1 antibodies ; etrolizumab Inhibition of the interaction between α4β7 integrins on T c… Details
S05 Angiogenesis cell proliferation; vascular permeability ozanimod The bioactive lipid S1P has been shown to activate NF-κB an… Details
S06 Anti-fibrosis fibrosis; tissue remodelling GS-5745; STNM01 Tissue remodelling and destruction in patients with IBD is … Details
S07 Blockade of cytokine Cytokine signalling apremilast; roflumilast; filgotinib; tofacitinib; ABT494; ABT-874; ustekinumab; isankizumab; LY-2525623; AMG139; MEDI2079; guselkumab Various T-cell subsets, their differentiation pathways and … Details
S08 Strengthening barrier function Modulation of barrier function phosphatidylcholine (lecithin); imiquimod; mongersen Escherichia coli Nissle (EcN) is a nonpathogenic Gram-negat… Details
S11 Improveming Intestinal Microecology the intestinal microbiota antibiotics; probiotics; prebiotics; postbiotics; synbiotics; fecal microbiota transplantation (FMT) The imbalance between beneficial bacteria and harmful patho… Details

Metformin Treatment: A Potential Cause of Megaloblastic Anemia in Patients with…

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Novel complementary coloprotective effects of metformin and MCC950 by modulatin…

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Ulcerative colitis (UC) is a chronic and relapsing inflammatory disorder, which has an increased incidence worldwide. The NLRP3 inflammasome has rece…

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PMID: 32156291
Year: 2020
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The gut microbiota is emerging as a prominent player in maintaining health through several metabolic and immune pathways. Dysregulation of gut microb…

Metformin Protects against LPS-Induced Intestinal Barrier Dysfunction by Activa…

PMID: 29969038
Year: 2018
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Metformin not only regulates energy metabolism but also participates in many cellular processes. In this study, we investigated the effect of metform…

Metformin inhibits inflammatory signals in the gut by controlling AMPK and p38 …

PMID: 29540537
Year: 2018
Relationship Type: Treatment Score: 6.3

Metformin, a hypoglycemic drug used for treatment of type 2 diabetes, regulates inflammatory pathways. By using several models of intestinal inflamma…

Metformin protects against intestinal barrier dysfunction via AMPKα1-dependent …

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Year: 2018
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Disruption of the intestinal epithelial barrier, that involves the activation of C-Jun N-terminal kinase (JNK), contributes to initiate and accelerat…

Metformin maintains mucosal integrity in experimental model of colitis by inhib…

PMID: 28821163
Year: 2017
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Metformin, an antidiabetic drug, is well known for its multifarious properties and its ability to modulate inflammatory cascade. Ulcerative colitis (…

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