Drug ID:Drug27
Drug Name:Metformin
CID:4091
DrugBank ID:DB00331
Modality:Small Molecule
Groups:approved
US Approved:YES
Other Approved:YES
Identifier: NCT05553704, , NCT05574387, , NCT03986996
Molecular Formula:C4H11N5
Molecular Weight:129.16 g/mol
Isomeric SMILES:CN(C)C(=N)N=C(N)N
Synonyms:metformin; 657-24-9; 1,1-Dimethylbiguanide; N,N-dimethylimidodicarbonimidic diamide; Fluamine; Metformine; Metiguanide; Imidodicarbonimidic diamide, N,N-dimethyl-; Dimethylbiguanide; Flumamine
Phase 0: 58
Phase 1: 745
Phase 2: 530
Phase 3: 564
Phase 4: 555
Description:Metformin is a biguanide antihyperglycemic agent used for treating non-insulin-dependent diabetes mellitus (NIDDM). It improves glycemic control by decreasing hepatic glucose production, decreasing glucose absorption and increasing insulin-mediated glucose uptake. Metformin is the only oral antihyperglycemic agent that is not associated with weight gain. Metformin may induce weight loss and is the drug of choice for obese NIDDM patients. When used alone, metformin does not cause hypoglycemia; however, it may potentiate the hypoglycemic effects of sulfonylureas and insulin. Its main side effects are dyspepsia, nausea and diarrhea. Dose titration and/or use of smaller divided doses may decrease side effects. Metformin should be avoided in those with severely compromised renal function (creatinine clearance < 30 ml/min), acute/decompensated heart failure, severe liver disease and for 48 hours after the use of iodinated contrast dyes due to the risk of lactic acidosis. Lower doses should be used in the elderly and those with decreased renal function. Metformin decreases fasting plasma glucose, postprandial blood glucose and glycosolated hemoglobin (HbA1c) levels, which are reflective of the last 8-10 weeks of glucose control. Metformin may also have a positive effect on lipid levels. In 2012, a combination tablet of linagliptin plus metformin hydrochloride was marketed under the name Jentadueto for use in patients when treatment with both linagliptin and metformin is appropriate.

Molecular Structure

2D Molecular Structure

Knowledge Graph

dtIDCIDCompound NameGene IDGene NameSpeciesPubMed IDsAction
dt248 4091 Metformin 5604 MAP2K1 Homo sapiens (human) None
dt249 4091 Metformin 6794 STK11 Homo sapiens (human) None
dt250 4091 Metformin 5728 PTEN Homo sapiens (human) None
dt251 4091 Metformin 5290 PIK3CA Homo sapiens (human) None
dt252 4091 Metformin 3265 HRAS Homo sapiens (human) None
dt253 4091 Metformin 5465 PPARA Homo sapiens (human) None
dt254 4091 Metformin 55244 SLC47A1 Homo sapiens (human) 37713619 Modulator
dt255 4091 Metformin 32 ACACB Homo sapiens (human) 37713619 Activator
dt256 4091 Metformin 2110 ETFDH Homo sapiens (human) Inhibitor
dt257 4091 Metformin 5564 PRKAB1 Homo sapiens (human) Inducer|Activator

  • No data available

Phase Distribution
Phase Description
  • Phase 0: Exploratory trials to assess drug behavior in humans
  • Phase 1: Safety trials to determine safe dosage range
  • Phase 2: Efficacy trials to evaluate therapeutic effects
  • Phase 3: Large-scale trials to confirm efficacy and safety
  • Phase 4: Post-marketing surveillance for long-term safety and efficacy

Trial IDTitlePhaseStatusSponsorIndicationsInterventions
NCT05574387 Metformin as Added on Therapy in Patients With Ulcerative Colitis PHASE2 RECRUITING Tanta University Inflammatory Bowel Diseases DRUG: Metformin Details
NCT05553704 Metformin in Patients With Ulcerative Colitis Treated With Mesalamine PHASE2 COMPLETED Tanta University Inflammatory Bowel Diseases DRUG: Metformin Details
NCT04750135 Assessment of Metformin as Adjuvant Therapy in Patients With Ulcerative Colitis PHASE2 UNKNOWN National Hepatology & Tropical Medicine Research Institute Ulcerative Colitis|Inflammatory Bowel Diseases DRUG: metformin 500 mg TID Oral Tablet|DRUG: Plac… Details
NCT05707429 Sexual Function and Quality of Life Among Patients Suffering From Inflammatory Bowel Disease(Inactive Stage) NULL COMPLETED Assiut University Sexual Function Disturbances|Inflammatory Bowel D… OTHER: The Arabic version of The International In… Details
NCT05706038 Impact of Adalimumab Withdrawal or Continuation on Severity of COVID-19 and Risk of IMID Relapse NULL COMPLETED IRCCS San Raffaele Inflammatory Bowel Diseases|Rheumatic Disorder DRUG: Adalimumab Details
NCT05687474 Baby Detect : Genomic Newborn Screening NULL COMPLETED Centre Hospitalier Universitaire de Liege Congenital Adrenal Hyperplasia|Familial Hyperinsu… None Details
NCT05668104 Jing Si Herbal Tea for Long-Coronavirus Disease(COVID) Gut-brain Interaction NA COMPLETED Buddhist Tzu Chi General Hospital Healthy Subjects|COVID-19 Pneumonia|Irritable Bow… DIETARY_SUPPLEMENT: Jing Si Herbal Tea Liquid Pac… Details
NCT05643534 Study to Assess Safety and Efficacy of Tenapanor for Treatment of IBS-C in Pediatric Patients 12 to Less Than 18 Years PHASE3 RECRUITING Ardelyx Irritable Bowel Syndrome With Constipation (IBS-C) DRUG: Tenapanor 50 MG|DRUG: Tenapanor 25 mg bid|D… Details
NCT05626023 A Study of Human TH-SC01 Cell Injection for Treating Perianal Fistulas in Patients With Crohn's Disease PHASE1|PHASE2 COMPLETED Jiangsu Topcel-KH Pharmaceutical Co., Ltd. Perianal Fistula|Crohn's Disease DRUG: Human TH-SC01 cell injection Details
NCT05588843 Dose-finding Study of SAR443122 in Adult Participants With Ulcerative Colitis PHASE2 ACTIVE_NOT_RECRUITING Sanofi Colitis Ulcerative DRUG: SAR443122|DRUG: Placebo Details
NCT05584735 Determining the Relationship Between Gut Microbiota and Immune Response to Influenza or COVID-19 Vaccine NULL COMPLETED University of Wisconsin, Madison Inflammatory Bowel Diseases BIOLOGICAL: Influenza vaccine|BIOLOGICAL: COVID-1… Details
NCT05573685 Basket Study (CT-100-002) to Evaluate the Effects of a DiNaMo™ Component Training NA COMPLETED Click Therapeutics, Inc. Rheumatoid Arthritis|Diabetic Neuropathy|Fibromya… DEVICE: DiNaMo Study App|DEVICE: Placebo App Details
NCT05542355 EXL01 in the Maintenance of Steroid-induced Clinical Response/Remission in Participants With Mild to Moderate Crohn's Disease PHASE1 TERMINATED Exeliom Biosciences Crohn Disease DRUG: EXL01|DRUG: Placebo|OTHER: SoC corticostero… Details
NCT05536440 A Study to Learn About Study Medicine Called PF-07261271 in Healthy People PHASE1 COMPLETED Pfizer Healthy DRUG: PF-07261271|DRUG: Placebo Details
NCT05528510 A Study of Guselkumab Therapy in Participants With Moderately to Severely Active Ulcerative Colitis PHASE3 ACTIVE_NOT_RECRUITING Janssen Research & Development, LLC Colitis, Ulcerative DRUG: Guselkumab Dose 1|DRUG: Guselkumab Dose 2|D… Details
NCT07161297 Remimazolam for Colonoscopy in IBD Patients PHASE4 NOT_YET_RECRUITING Humanitas Clinical and Research Center IBD (Inflammatory Bowel Disease) DRUG: Intravenous remimazolam (5 mg initially, wi… Details
NCT05507931 Broccoli Sprouts for Mild Ulcerative Colitis NA COMPLETED University of Michigan Ulcerative Colitis|Ulcerative Colitis Chronic Mild DIETARY_SUPPLEMENT: 1 Serving of broccoli sprouts… Details
NCT05507203 ABTECT-1 - ABX464 Treatment Evaluation for Ulcerative Colitis Therapy -1 PHASE3 COMPLETED Abivax S.A. Ulcerative Colitis DRUG: ABX464|DRUG: Placebo Details
NCT07156929 Kinetics and Metabolism of Nicotinamide Provided as a Dietary Supplementation NA COMPLETED University Hospital Schleswig-Holstein Respiratory Infection (for Example, Pneumonia, Br… DIETARY_SUPPLEMENT: Controlled-ileocolonic-releas… Details
NCT05466890 Phase 2a to Evaluate PL-8177 in Subjects with Active Ulcerative Colitis (UC) PHASE2 ACTIVE_NOT_RECRUITING Palatin Technologies, Inc Ulcerative Colitis|Ulcerative Colitis Acute|Ulcer… DRUG: PL8177 Placebo|DRUG: PL8177 Details

Disease IDDisease NameDefinitionCategoryRelated DrugsMechanism
1.0 Crohn's disease An intestinal disease that involves inflammation located_in intestine. disease of anatomical entity gastrointestinal system disease, intestinal disease, inflammatory bowel disease Obiltoxaximab; Budesonide; Hydrocortisone acetate; Sulfasalazine; Ursodeoxycholic acid; Pegunigalsidase alfa; Imiglucerase; Bictegravir; Taliglucerase alfa; Etelcalcetide; Cimetidine; Desonide Crohn's disease is a relapsing systemic inflammatory diseas… Details

Strategy IDTherapeutic StrategySynonymsRelated DrugsMechanism
S01 Anti-inflammatory inflammatory 5-Aminosalicylates (5-ASAs); corticosteroids Crohn's disease and ulcerative colitis are the two main com… Details
S02 Immunosuppression Classic immunosuppressive drugs azathioprine; 6-mercaptopurine; methotrexate; ciclosporin-A; tacrolimus Ciclosporin-A and tacrolimus bind to specific intracellular… Details
S03 Anti-TNF agents Tumor necrosis factor infliximab; adalimumab; golimumab; certolizumab pegol TNF is produced by various immune and non-immune cells in t… Details
S04 T-cell homing and retention T-cell trafficking vedolizumab; anti-MAdCAM1 antibodies ; etrolizumab Inhibition of the interaction between α4β7 integrins on T c… Details
S05 Angiogenesis cell proliferation; vascular permeability ozanimod The bioactive lipid S1P has been shown to activate NF-κB an… Details
S06 Anti-fibrosis fibrosis; tissue remodelling GS-5745; STNM01 Tissue remodelling and destruction in patients with IBD is … Details
S07 Blockade of cytokine Cytokine signalling apremilast; roflumilast; filgotinib; tofacitinib; ABT494; ABT-874; ustekinumab; isankizumab; LY-2525623; AMG139; MEDI2079; guselkumab Various T-cell subsets, their differentiation pathways and … Details
S08 Strengthening barrier function Modulation of barrier function phosphatidylcholine (lecithin); imiquimod; mongersen Escherichia coli Nissle (EcN) is a nonpathogenic Gram-negat… Details
S11 Improveming Intestinal Microecology the intestinal microbiota antibiotics; probiotics; prebiotics; postbiotics; synbiotics; fecal microbiota transplantation (FMT) The imbalance between beneficial bacteria and harmful patho… Details

Metformin Treatment: A Potential Cause of Megaloblastic Anemia in Patients with…

PMID: 33116733
Year: 2020
Relationship Type: Treatment Score: 6.5

INTRODUCTION: Vitamin B12 (cobalamin) deficiency is a frequent cause of megaloblastic anemia, manifested through various symptoms. Screening for this…

Novel complementary coloprotective effects of metformin and MCC950 by modulatin…

PMID: 32594364
Year: 2021
Relationship Type: Treatment Score: 6.5

Ulcerative colitis (UC) is a chronic and relapsing inflammatory disorder, which has an increased incidence worldwide. The NLRP3 inflammasome has rece…

Metformin effect on gut microbiota: insights for HIV-related inflammation

PMID: 32156291
Year: 2020
Relationship Type: Treatment Score: 6.5

The gut microbiota is emerging as a prominent player in maintaining health through several metabolic and immune pathways. Dysregulation of gut microb…

Metformin Protects against LPS-Induced Intestinal Barrier Dysfunction by Activa…

PMID: 29969038
Year: 2018
Relationship Type: Treatment Score: 6.3

Metformin not only regulates energy metabolism but also participates in many cellular processes. In this study, we investigated the effect of metform…

Metformin inhibits inflammatory signals in the gut by controlling AMPK and p38 …

PMID: 29540537
Year: 2018
Relationship Type: Treatment Score: 6.3

Metformin, a hypoglycemic drug used for treatment of type 2 diabetes, regulates inflammatory pathways. By using several models of intestinal inflamma…

Metformin protects against intestinal barrier dysfunction via AMPKα1-dependent …

PMID: 29148173
Year: 2018
Relationship Type: Mechanism Score: 6.3

Disruption of the intestinal epithelial barrier, that involves the activation of C-Jun N-terminal kinase (JNK), contributes to initiate and accelerat…

Metformin maintains mucosal integrity in experimental model of colitis by inhib…

PMID: 28821163
Year: 2017
Relationship Type: Treatment Score: 6.3

Metformin, an antidiabetic drug, is well known for its multifarious properties and its ability to modulate inflammatory cascade. Ulcerative colitis (…

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