Drug ID:Drug34
Drug Name:Pentoxifylline
CID:4740
DrugBank ID:DB00806
Modality:Small Molecule
Groups:approved|investigational
US Approved:YES
Other Approved:YES
Identifier: NCT01438372
Molecular Formula:C13H18N4O3
Molecular Weight:278.31 g/mol
Isomeric SMILES:CC(=O)CCCCN1C(=O)C2=C(N=CN2C)N(C1=O)C
Synonyms:pentoxifylline; 6493-05-6; Oxpentifylline; Pentoxifyllin; Pentoxyphylline; Pentoxiphyllium; Vazofirin; 3,7-Dimethyl-1-(5-oxohexyl)xanthine; Dimethyloxohexylxanthine; Pentoxiphyllin
Phase 0: 8
Phase 1: 17
Phase 2: 70
Phase 3: 41
Phase 4: 25
Description:A methylxanthine derivative that inhibits phosphodiesterase and affects blood rheology. It improves blood flow by increasing erythrocyte and leukocyte flexibility. It also inhibits platelet aggregation. Pentoxifylline modulates immunologic activity by stimulating cytokine production. [PubChem]

Molecular Structure

2D Molecular Structure

Knowledge Graph

dtIDCIDCompound NameGene IDGene NameSpeciesPubMed IDsAction
dt315 4740 Pentoxifylline 3689 ITGB2 Homo sapiens (human) None
dt316 4740 Pentoxifylline 5142 PDE4B Homo sapiens (human) None
dt317 4740 Pentoxifylline 27115 PDE7B Homo sapiens (human) Inhibitor
dt318 4740 Pentoxifylline 2670 GFAP Homo sapiens (human) None
dt319 4740 Pentoxifylline 136 ADORA2B Homo sapiens (human) 12014951 Antagonist
dt320 4740 Pentoxifylline 5243 ABCB1 Homo sapiens (human) 33775688 [pentoxifylline co-treated with doxorubicin] results in decreased expression of ABCB1 protein|pentoxifylline results in decreased expression of ABCB1 protein
dt321 4740 Pentoxifylline 4363 ABCC1 Homo sapiens (human) 33775688 [pentoxifylline co-treated with doxorubicin] results in decreased expression of ABCC1 protein
dt322 4740 Pentoxifylline 43 ACHE Rattus norvegicus (Norway rat) 11981227 Pentoxifylline results in decreased activity of ACHE protein
dt323 4740 Pentoxifylline 59 ACTA2 Homo sapiens (human) 18207697 Pentoxifylline promotes the reaction [carbon tetrachloride results in increased expression of ACTA2 mrna]
dt324 4740 Pentoxifylline 59 ACTA2 Rattus norvegicus (Norway rat) 14996430 Pentoxifylline results in decreased expression of ACTA2 protein

  • No data available

Phase Distribution
Phase Description
  • Phase 0: Exploratory trials to assess drug behavior in humans
  • Phase 1: Safety trials to determine safe dosage range
  • Phase 2: Efficacy trials to evaluate therapeutic effects
  • Phase 3: Large-scale trials to confirm efficacy and safety
  • Phase 4: Post-marketing surveillance for long-term safety and efficacy

Trial IDTitlePhaseStatusSponsorIndicationsInterventions
NCT05575505 Phosphodiesterase Inhibitors, Pentoxifylline, as Adjunctive Therapy in Patients With Ulcerative Colitis. PHASE2 RECRUITING Tanta University Inflammatory Bowel Diseases DRUG: Pentoxifylline 400 MG Details
NCT05558761 Pentoxifylline as Adjunctive Therapy in Patients With Ulcerative Colitis PHASE2 RECRUITING Tanta University Inflammatory Bowel Diseases DRUG: Pentoxifylline 400 MG Details
NCT02953275 Synergistic Effect of Vedolizumab and Pentoxifylline in the Management of Patients With Inflammatory Bowel Disease EARLY_PHASE1 Not recruiting University of Miami Crohn Disease Drug: vedolizumab;Drug: Pentoxifylline;Drug: plac… Details
NCT04857112 Study Evaluating Efficacy and Safety of Amiselimod (MT-1303) in Mild to Moderate Ulcerative Colitis PHASE2 ACTIVE_NOT_RECRUITING Bausch Health Americas, Inc. Ulcerative Colitis DRUG: Low Dose MT-1303|DRUG: High Dose MT-1303|DR… Details
NCT02447302 Safety and Efficacy of Etrasimod (APD334) in Patients With Ulcerative Colitis PHASE2 COMPLETED Arena Pharmaceuticals Ulcerative Colitis DRUG: Etrasimod|DRUG: Placebo Details
NCT02762500 An Efficacy and Safety Study of LYC-30937-EC in Subjects With Active Ulcerative Colitis PHASE2 COMPLETED Lycera Corp. Colitis, Ulcerative DRUG: LYC-30937-EC|DRUG: Placebo Details
NCT04677179 A Study of LY3471851 in Adult Participants With Moderately to Severely Active Ulcerative Colitis (UC) PHASE2 TERMINATED Nektar Therapeutics Colitis, Ulcerative DRUG: LY3471851|DRUG: Placebo Details
NCT03849599 A Study to Evaluate the Safety of PRV-300 in Adult Subjects With Moderately to Severely Active Ulcerative Colitis PHASE1 COMPLETED Provention Bio, Inc. Ulcerative Colitis BIOLOGICAL: PRV-300|BIOLOGICAL: Placebo Details
NCT02611830 Efficacy and Safety of Vedolizumab Subcutaneously (SC) as Maintenance Therapy in Ulcerative Colitis PHASE3 COMPLETED Takeda Colitis, Ulcerative DRUG: Vedolizumab 300 mg IV|DRUG: Placebo IV|DRUG… Details
NCT05807971 Assessment of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of ATH-063 in Healthy Subjects PHASE1 COMPLETED Athos Therapeutics Inc Inflammatory Bowel Diseases|Crohn Disease|Ulcerat… DRUG: ATH-063|DRUG: Placebo Details
NCT02039505 Phase III Study of MLN0002 (300 mg) in the Treatment of Ulcerative Colitis PHASE3 COMPLETED Takeda Ulcerative Colitis DRUG: Vedolizumab|DRUG: Vedolizumab placebo Details
NCT05076175 A Study Investigating Oral Ozanimod (RPC1063) in Pediatric Participants With Moderate to Severe Active Ulcerative Colitis PHASE2|PHASE3 RECRUITING Bristol-Myers Squibb Colitis, Ulcerative DRUG: Ozanimod Details
NCT06636656 A Study to Test Whether BI 3032950 Helps People With Ulcerative Colitis PHASE2 RECRUITING Boehringer Ingelheim Ulcerative Colitis DRUG: BI 3032950 intravenous (Part A)|DRUG: BI 30… Details
NCT04996797 A Phase 2 Safety and Efficacy Study of Tulisokibart (MK-7240/PRA023) in Subjects With Moderately to Severely Active Ulcerative Colitis (MK-7240-005) PHASE2 ACTIVE_NOT_RECRUITING Prometheus Biosciences, Inc., a subsidiary of Merck & Co., Inc. (Rahway, New Jersey USA) Ulcerative Colitis DRUG: Tulisokibart|DEVICE: Companion Diagnostic (… Details
NCT01959282 A Study of Safety and Effectiveness of JNJ-54781532 in Patients With Moderately to Severely Active Ulcerative Colitis PHASE2 COMPLETED Janssen Research & Development, LLC Colitis, Ulcerative DRUG: Placebo|DRUG: JNJ-54781532 25 mg once daily… Details
NCT06381518 Switching From Intravenous to Subcutaneous Infliximab in Adult Patients With Inflammatory Bowel Disease None ENROLLING_BY_INVITATION Zuyderland Medisch Centrum IBD|Infliximab|Crohn Disease|Ulcerative Colitis OTHER: Switch to SC CT-P13. Details
NCT00628433 Safety and Pharmacokinetics Study of HE3286 in Patients With Active, Mild-to-Moderate Ulcerative Colitis PHASE1|PHASE2 COMPLETED Harbor Therapeutics Ulcerative Colitis DRUG: Placebo|DRUG: HE3286 Details
NCT01877577 Supplementation of Vitamin D3 in Patients With Inflammatory Bowel Diseases and Hypovitaminosis D None COMPLETED University of California, San Francisco Crohn's Disease (CD)|Ulcerative Colitis (UC) DIETARY_SUPPLEMENT: Vitamin D3 Details
NCT00317356 A Dose-finding Study of OPC-6535 in Patients With Active Ulcerative Colitis PHASE2 TERMINATED Otsuka Pharmaceutical Co., Ltd. Colitis, Ulcerative DRUG: OPC-6535(Tetomilast) Details
NCT05019742 Evaluation of SPH3127 in Patients With Mild-to-Moderate Ulcerative Colitis PHASE2 RECRUITING Shanghai Pharma Biotherapeutics USA Inc. Ulcerative Colitis DRUG: SPH3127|DRUG: Placebo Details

Disease IDDisease NameDefinitionCategoryRelated DrugsMechanism
No data available

Strategy IDTherapeutic StrategySynonymsRelated DrugsMechanism
S07 Blockade of cytokine Cytokine signalling apremilast; roflumilast; filgotinib; tofacitinib; ABT494; ABT-874; ustekinumab; isankizumab; LY-2525623; AMG139; MEDI2079; guselkumab Various T-cell subsets, their differentiation pathways and … Details

Pentoxifylline in patients with ulcerative colitis treated with mesalamine by m…

PMID: 39192162
Year: 2024
Relationship Type: Treatment Score: 9.5

BACKGROUND: Ulcerative colitis (UC) is an inflammatory bowel disease (IBD) that lasts a long time and has a variety of causes. AIM: The primary aim o…

Therapeutic Potential of the Combination of Pentoxifylline and Vitamin-E in Inf…

PMID: 36012952
Year: 2022
Relationship Type: Treatment Score: 9.5

BACKGROUND: Although intestinal fibrosis is a consequence of recurrent inflammation in Inflammatory bowel disease (IBD), alleviating inflammation alo…

Combining Pentoxifylline With Vedolizumab for Crohn's Disease: Results of a Ran…

PMID: 35642747
Year: 2022
Relationship Type: Treatment Score: 9.5

BACKGROUND AND AIMS: The efficacy of current biologics may be limited by targeting only one pathway. Pentoxifylline [PTX] interferes with tumour necr…

A Potential Role of Ethosuximide and Pentoxifylline in Relieving Abdominal Pain…

PMID: 35221706
Year: 2022
Relationship Type: Treatment Score: 9.5

BACKGROUND AND PURPOSE: Irritable bowel syndrome (IBS) is defined as an association of chronic abdominal pain with bowel habit abnormalities, without…

Randomised single centre double-blind placebo controlled phase II trial of Toco…

PMID: 35093409
Year: 2022
Relationship Type: Treatment Score: 9.5

BACKGROUND: Preclinical data suggest that combined gamma-tocotrienol with pentoxifylline ameliorates radiotherapy-induced gastrointestinal damage. AI…

Pentoxifylline, a nonselective phosphodiesterase inhibitor, in adjunctive thera…

PMID: 34775240
Year: 2022
Relationship Type: Treatment Score: 9.5

BACKGROUND: Irritable bowel syndrome (IBS) is a functional gastrointestinal condition marked by chronic bowel pain or discomfort, as well as changes …

Inhibitory effects of pentoxifylline on inflammation-related tumorigenesis in r…

PMID: 30338039
Year: 2018
Relationship Type: Treatment Score: 6.3

Biological agents have proven clinical efficacy in the treatment of ulcerative colitis (UC). Their adverse effects have also been studied in a subst…