Drug ID:Drug39
Drug Name:Thalidomide
CID:5426
DrugBank ID:DB01041
Modality:Small Molecule
Groups:approved|investigational|withdrawn
US Approved:YES
Other Approved:YES
Identifier: NCT06382519, , NCT00720538
Molecular Formula:C13H10N2O4
Molecular Weight:258.23 g/mol
Isomeric SMILES:C1CC(=O)NC(=O)C1N2C(=O)C3=CC=CC=C3C2=O
Synonyms:thalidomide; 50-35-1; Contergan; Distaval; Pantosediv; Softenon; Kevadon; Theophilcholine; Algosediv; Corronarobetin
Phase 0: 2
Phase 1: 33
Phase 2: 265
Phase 3: 97
Phase 4: 20
Description:A piperidinyl isoindole originally introduced as a non-barbiturate hypnotic, but withdrawn from the market due to teratogenic effects. It has been reintroduced and used for a number of immunological and inflammatory disorders. Thalidomide displays immunosuppresive and anti-angiogenic activity. It inhibits release of tumor necrosis factor-alpha from monocytes, and modulates other cytokine action. [PubChem]

Molecular Structure

2D Molecular Structure

Knowledge Graph

dtIDCIDCompound NameGene IDGene NameSpeciesPubMed IDsAction
dt355 5426 Thalidomide 5743 PTGS2 Homo sapiens (human) None
dt356 5426 Thalidomide 2263 FGFR2 Homo sapiens (human) None
dt357 5426 Thalidomide 7124 TNF Homo sapiens (human) None
dt358 5426 Thalidomide 8451 CUL4A Homo sapiens (human) Inhibitor
dt359 5426 Thalidomide 51185 CRBN Homo sapiens (human) 20223979 Binding
dt360 5426 Thalidomide 2651 GCNT2 Mus musculus (house mouse) 26217789 Thalidomide results in decreased expression of GCNT2 mRNA
dt361 5426 Thalidomide 2638 GC Gallus gallus (chicken) 28892372 Thalidomide results in decreased expression of GC mRNA
dt362 5426 Thalidomide 6241 RRM2 Homo sapiens (human) 18720364 [azacitidine co-treated with thalidomide] affects the expression of RRM2 mRNA

  • No data available

Phase Distribution
Phase Description
  • Phase 0: Exploratory trials to assess drug behavior in humans
  • Phase 1: Safety trials to determine safe dosage range
  • Phase 2: Efficacy trials to evaluate therapeutic effects
  • Phase 3: Large-scale trials to confirm efficacy and safety
  • Phase 4: Post-marketing surveillance for long-term safety and efficacy

Trial IDTitlePhaseStatusSponsorIndicationsInterventions
NCT06382519 Thalidomide Therapy for VEOIBD None RECRUITING Children's Hospital of Fudan University Inflammatory Bowel Diseases DRUG: Thalidomide Details
NCT00720538 Thalidomide in Pediatric Inflammatory Bowel Diseases. PHASE3 COMPLETED IRCCS Burlo Garofolo Inflammatory Bowel Diseases|Crohn's Disease|Ulcer… DRUG: Thalidomide|DRUG: placebo Details
ISRCTN23541842 The auxiliary diagnostic value of fissured tongue on axial and peripheral joint dysfunction in Ankylosing Spondylitis Not Available Not Recruiting Zhejiang University Of Chinese Medicine Ankylosing spondylitis Musculoskeletal Diseases … Participants are screened and undergo a clinical … Details
EUCTR2005-005414-20-IT Randomized controlled double-blind Vs. placebo multicentre study on the safety and effectiveness of thalidomide in the treatment of refractory Crohn s disease and ulcerative colitis. - Thalidomide and IBD Not Available Authorised ISTITUTO PER L INFANZIA BURLO GAROFOLO Inflammatory Bowel Disease Crohn Disease, Ulcera… Trade Name: Thalidomide Pharmion Pharmaceutical F… Details

Disease IDDisease NameDefinitionCategoryRelated DrugsMechanism
No data available

Strategy IDTherapeutic StrategySynonymsRelated DrugsMechanism
No data available

Thalidomide for inflammatory bowel disease: Systematic review

PMID: 27472695
Year: 2016
Relationship Type: Treatment Score: 6.3

BACKGROUND: Thalidomide is an immunomodulatory drug used in the experimental treatment of refractory Crohn disease and ulcerative colitis. We aimed t…

Effect of Thalidomide on Clinical Remission in Children and Adolescents with Ul…

PMID: 26185909
Year: 2015
Relationship Type: Treatment Score: 6.3

BACKGROUND: In a randomized controlled trial, thalidomide has shown to be effective in refractory Crohn's disease in children. This pilot study aimed…

Thalidomide as rescue therapy for acute severe ulcerative colitis

PMID: 24992607
Year: 2014
Relationship Type: Treatment Score: 6.3

INTRODUCTION: Acute severe exacerbations of Ulcerative Colitis (UC) represent a medical emergency in children and adults. Intravenous steroids remain…

Efficacy of thalidomide on trinitrobenzene sulfonate-induced colitis in young r…

PMID: 24931258
Year: 2014
Relationship Type: Treatment Score: 6.3

BACKGROUND: Thalidomide could relieve clinical symptoms and intestinal mucosal lesions effectively in children with refractory inflammatory bowel dis…

[An analysis of adverse drug reactions of thalidomide in treatment of immune-re…

PMID: 24314159
Year: 2013
Relationship Type: Treatment Score: 6.1

OBJECTIVE: To investigate the safety of thalidomide in the treatment of immune-related bowel diseases for providing clinical reference. METHODS: Thir…

Effect of thalidomide on clinical remission in children and adolescents with re…

PMID: 24281461
Year: 2013
Relationship Type: Treatment Score: 6.1

IMPORTANCE: Pediatric-onset Crohn disease is more aggressive than adult-onset disease, has high rates of resistance to existing drugs, and can lead t…

Idiopathic ileocolitis with perforation associated with HIV infection: thalidom…

PMID: 23155107
Year: 2012
Relationship Type: Treatment Score: 6.1

Idiopathic cutaneous ulcers, oesophageal ulcers and severe ulcerative ileocolitis occurred in a human immunodeficiency virus (HIV)-infected patient e…

Thalidomide induces mucosal healing in Crohn's disease: case report

PMID: 22174554
Year: 2011
Relationship Type: Treatment Score: 6.1

Crohn's disease is a chronic inflammatory disorder of the gastrointestinal tract that is defined by relapsing and remitting episodes. Tumor necrosis …

Effect of combination of thalidomide and sulfasalazine in experimentally induce…

PMID: 21941940
Year: 2011
Relationship Type: Treatment Score: 6.1

Thalidomide provided significant protection against tri nitro benzene sulfonic acid induced colitis. Combination therapy also reduced colonic inflamm…

Thalidomide use and outcomes in pediatric patients with Crohn disease refractor…

PMID: 21681114
Year: 2012
Relationship Type: Treatment Score: 6.1

OBJECTIVE: The aim of the study was to evaluate thalidomide as rescue therapy for pediatric patients with severe refractory Crohn disease (CD) who fa…

Treatment of pediatric refractory Crohn's disease with thalidomide

PMID: 21455327
Year: 2011
Relationship Type: Treatment Score: 6.1

AIM: To assess the efficacy and tolerability of thalidomide in pediatric Crohn's disease (CD). METHODS: Six patients with refractory CD received thal…

[Thalidomide as immunomodulatory drug: pharmacological actions and its indicati…

PMID: 21048383
Year: 2010
Relationship Type: Treatment Score: 6.1

Thalidomide was developed in the 1950s as a sedative drug and withdrawn in 1961 because of its teratogenic effects, but has been rediscovered as an i…

Thalidomide inhibits inflammatory and angiogenic activation of human intestinal…

PMID: 19926820
Year: 2010
Relationship Type: Treatment Score: 6.1

Comment in Dig Liver Dis. 2005 Jun;37(6):391-3. INTRODUCTION: Despite the explosion of biological therapies, the old immunosuppressants continu…

Showing 21-33 of 33 articles